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Ultragenyx Pharmaceutical Inc. news in 2025

Ultragenyx Pharmaceutical Inc.'s news releases, calls and decks from 2025, newest first.

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Ultragenyx Completes Rolling Submission of Biologics License Application (BLA) to U.S. FDA for DTX401 AAV Gene Therapy for Glycogen Storage Disease Type Ia (GSDIa)

December 29, 2025

Ultragenyx Announces Phase 3 Orbit and Cosmic Results for Setrusumab (UX143) in Osteogenesis Imperfecta

December 28, 2025

Tactical Resources Announces Share Consolidation

December 3, 2025

Ultragenyx to Participate in Investor Conferences in December

November 23, 2025

Ultragenyx Reports Third Quarter 2025 Financial Results and Corporate Update

November 3, 2025

Ultragenyx Announces Sale of a Portion of Future North American Royalties on Crysvita® (burosumab) for $400 Million to OMERS Life Sciences

November 3, 2025

Ultragenyx Announces First Patient Dosed in Aurora Study Evaluating GTX-102 in Additional Angelman Syndrome Genotypes and Age Groups

October 29, 2025

Ultragenyx to Host Conference Call for Third Quarter 2025 Financial Results and Corporate Update

October 27, 2025

Ultragenyx Appoints Eric Olson as Chief Business Officer and Executive Vice President

September 29, 2025

Ultragenyx Announces Positive Longer-term Data from Phase 3 Study of DTX401 AAV Gene Therapy for the Treatment of Glycogen Storage Disease Type Ia (GSDIa)

September 7, 2025

Ultragenyx to Participate at Investor Conferences in September

August 28, 2025

Ultragenyx Initiates Rolling Submission of Biologics License Application (BLA) to U.S. FDA for DTX401 AAV Gene Therapy for the Treatment of Glycogen Storage Disease Type Ia (GSDIa)

August 17, 2025

Ultragenyx Reports Second Quarter 2025 Financial Results and Corporate Update

August 5, 2025

Ultragenyx Completes Enrollment of Phase 3 Aspire Study Evaluating GTX-102 for the Treatment of Angelman Syndrome

July 30, 2025

Ultragenyx to Host Conference Call for Second Quarter 2025 Financial Results and Corporate Update

July 29, 2025

New Pedestrian Access from Inner Belt to East Somerville MBTA Station Now Open to the Public

July 16, 2025

Health Canada Extends the Approval of Evkeeza® (evinacumab) to Children as Young as 6-months Old with Homozygous Familial Hypercholesterolemia (HoFH)

July 14, 2025

Ultragenyx Receives Complete Response Letter from FDA for UX111 AAV Gene Therapy to Treat Sanfilippo Syndrome Type A (MPS IIIA)

July 10, 2025

Ultragenyx and Mereo BioPharma Announce UX143 Phase 3 Orbit Study for Osteogenesis Imperfecta Progressing to Final Analysis

July 8, 2025

Ultragenyx Receives Breakthrough Therapy Designation for GTX-102 in Angelman Syndrome

June 26, 2025

Ultragenyx to Participate at Goldman Sachs 46th Annual Global Healthcare Conference

June 2, 2025

Ultragenyx Underscores Continued Commitment to Rare Disease Innovation with 2024 Impact Report

May 13, 2025

Ultragenyx to Participate at Bank of America’s 2025 Healthcare Conference

May 6, 2025

Ultragenyx Reports First Quarter 2025 Financial Results and Corporate Update

May 5, 2025

Ultragenyx to Host Conference Call for First Quarter 2025 Financial Results and Corporate Update

April 29, 2025

Ultragenyx to Participate at Investor Conferences in March

February 23, 2025

Ultragenyx Announces FDA Acceptance and Priority Review of the Biologics License Application (BLA) for UX111 AAV Gene Therapy to Treat Sanfilippo Syndrome Type A (MPS IIIA)

February 17, 2025

Ultragenyx Reports Fourth Quarter and Full Year 2024 Financial Results and Corporate Update

February 12, 2025

Ultragenyx to Host Conference Call for Fourth Quarter and Full-Year 2024 Financial Results and Corporate Update

February 5, 2025

Ultragenyx Announces New Data Demonstrating that Treatment with UX111 AAV Gene Therapy Significantly Improved Clinical Function Across Multiple Developmental Domains in Children with Sanfilippo Syndrome Type A (MPS IIIA) Correlated with Sustained Redu...

February 4, 2025

Ultragenyx Reports Preliminary 2024 Revenue, Financial Guidance for 2025, Pipeline Updates, and 2025 Milestones

January 11, 2025

Ultragenyx to Present at the 43rd Annual J.P. Morgan Healthcare Conference

January 5, 2025

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