Press release
Zevra Therapeutics Celebrates and Supports Global Niemann-Pick Disease Awareness Day on October 19th and Niemann-Pick Disease Awareness Month Throughout October
CELEBRATION, Fla., Oct. 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA), a rare disease therapeutics company, proudly supports the
About this update from Zevra Therapeutics, Inc.
[{"type":"text","content":"CELEBRATION, Fla., Oct. 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA), a rare disease therapeutics company, proudly supports the Niemann-Pick community on Global Niemann-Pick Disease Awareness Day and throughout Niemann-Pick Disease Awareness Month. Patient organizations like the International Niemann-Pick Disease Alliance (INPDA) and the National Niemann-Pick Disease Foundation (NNPDF) provide essential support for people living with Niemann-Pick disease type C (NPC) and their families and advocate for needed treatments. “So many members of the advocacy community around the world work tirelessly to support people who live with NPC and raise awareness of this devastating disease. At NNPDF, we welcome the opportunities to collaborate with industry partners like Zevra that are advancing promising research that can lead to new treatments that drive change and hope for the NPC community,” said Joslyn Crowe, Executive Director at NNPDF and Vice President of INPDA. “Throughout the year and especially during October where we observe Global Niemann-Pick Awareness Day and Niemann-Pick Awareness Month, we join with leaders from industry and our colleagues from the International Niemann-Pick Disease Alliance to help others understand the challenges associated with the condition and the future potential to provide needed relief to patients and families.” “NPC remains a condition with no approved treatment options in the U.S.,” said Daniel Gallo, Ph.D., Senior Vice President of Medical Affairs and Advocacy at Zevra. “It is an ultra-rare, genetic, relentlessly progressive neurodegenerative disease impacting approximately 1 in 100,000 live births. At Zevra we are focused on working closely with the advocacy community for the benefit of people living with NPC and their families.” Zevra remains committed to working with INPDA, NNPDF and the full NPC community to advance therapeutic options for this rare, neurodegenerative disease and devastating condition. Zevra also remains committed to patients receiving access to the Company’s investigational treatment, arimoclomol, through the ongoing Expanded Access Program (EAP), which is currently active in the United States and other European countries. About Niemann-Pick Disease Type C (NPC):Niemann-Pick disease type C (NPC) is an ultra-rare, progressive, neurodegenerative lysos...