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Modalis Announces Publication in Human Gene Therapy of Study Demonstrating Efficient LAMA1 Gene Activation for the Treatment of LAMA2-CMD

TOKYO & WALTHAM, Mass., December 25, 2025--Modalis Therapeutics Corporation (TOKYO: 4883) today announced that its research article titled "Efficient LAMA1 gene activation by epigenome editing as a therapeutic approach for LAMA2-CMD" has been published in the peer-reviewed journal Human Gene Therapy.

articleModalis Therapeutics CorporationDecember 24, 20253/company/modalis-therapeutics-corporation/news/modalis-announces-publication-in-human-gene-therapy-of-study-demonstrating-efficient-lama1-gene-activation-for-the-treatment-of-lama2-cmd
Modalis Announces Publication in Human Gene Therapy of Study Demonstrating Efficient LAMA1 Gene Activation for the Treatment of LAMA2-CMD

About this update from Modalis Therapeutics Corporation

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More updates from Modalis Therapeutics Corporation

Human Gene TherapyModalis Therapeuticsgene activationTetsuya Yamagatacongenital muscular dystrophygene replacementmuscle histologymuscle functionactivationinvestigational new drug applicationtherapeutic approachepigenome editing